Dr. Wang and his team at CHOC are participating in a clinical trial of a drug intended to treat a rare pediatric disease called MPS IIIA.
CHOC receives $8 million to advance research for rare disorder
An $8 million gift from the Foundation of Caring will help CHOC advance research for a rare lysosomal storage disorder, Pompe Disease.
CHOC Resident Follows in His Father’s Footsteps
Dr. Tim Hicks jokingly calls himself “Hicks 2.0,” a proud nod to his CHOC pulmonologist father, Dr. David Hicks.
William, Jeff and Jennifer Gross Family Foundation donates $2 million to CHOC’s Neonatal Intensive Care Unit
The recent gift rounds the Foundation’s support of CHOC’s neonatal services to $7 million in the past 12 months.
CHOC performs first in-human gene therapy dosing for MPS I
CHOC clinicians recently administered the first ever in-human dosing of gene therapy for Hurler Syndrome, a rare lysosomal storage disease.
Journey to a rare diagnosis: Colten’s story
A CHOC PICU nurse tells the story of her son, Colten, who received a rare Alström Syndrome diagnosis with the help of specialists at CHOC.
