The 2025 administration of gene therapy to treat sickle cell disease marked more than an historic first for Rady Children’s Health Orange County. It also changed the trajectory of a young adult’s life and capped a two-decade journey for the physician and the hematology team who delivered it.
Mi4 summer internship program is a proven career pipeline for patients, too
This year, more than 1,140 students applied for 75 internship positions, a reflection of both the program’s reputation and the growing interest among young people who want early exposure to healthcare.
First clinical research coordinator interns graduate from novel pediatric hospital program
Through a combination of formal instruction, mentorship, shadowing, and active participation in research activities, the CRC interns gained practical skills that cannot be fully taught in a classroom setting or abbreviated program.
Shaping the future of pediatric gene therapy
Learn how Rady Children’s Health Orange County investigates gene therapy to treat childhood diseases, including Hurler syndrome, liver cancer and more.
AI use across Rady Children’s Health Orange County is anchored in education, ethical use, and innovation
Now that artificial intelligence (AI) is everywhere, how does a pediatric healthcare system responsibly use the rapidly evolving technology for good? Rady Children’s Hospital Orange County has adopted a multi-layered approach involving leading-edge clinical, operational, and research-focused applications, with education and robust governance at the core to ensure that AI is incorporated into the hospital […]
‘Something better’? Gene therapy’s potential to treat Hurler syndrome
Discover how Rady Children’s Health Orange County is studying gene therapy as a less burdensome treatment alternative for children with Hurler syndrome.







