The CHOC Research Institute aims to pave the way for innovation in pediatric treatments with strategic academic partnerships.
CHOC is at the forefront of research for deep brain stimulation (DBS), a treatment for used on a small subset of patients, but this new work can lead to breakthroughs that potentially could affect millions.
Grant’s support will help advance gene-therapy treatment for the rare lysosomal storage disease mucopolysaccharidosis type I (MPS I).
Max, CHOC patient with acute lymphoblastic leukemia (ALL), participates in cancer research trials to improve outcomes and treatments.
Colorful comics aid young patients in understanding and providing assent for participation in research studies to advance treatments.
Parent provides powerful testimony at second-annual CHOC and UCI Rare Disease Symposium & Family Conference