“Every question we ask, every study we undertake, and every breakthrough we pursue begins with a single patient – the child whose story sparks curiosity, inspires discovery, and drives progress.”
CHOC-affiliated blood disorder center administers landmark gene therapy infusion for hemophilia
The center becomes the first in the country to administer a commercial gene therapy infusion to treat Hemophilia A, the common disorder affecting males.
‘We will have a better tomorrow for these kids’
Parent provides powerful testimony at second-annual CHOC and UCI Rare Disease Symposium & Family Conference
Second-annual CHOC-UCI Rare Diseases Symposium set for March 10, 2023
At the annual symposium, hundreds will gather to share about advances in rare disease research and a unifying theme: hope.
Device for patients with GI issues showing promise in treating Post-Concussion Syndrome
CHOC doctors discover the possible efficacy of treating PCS with the GI device IB-Stim. A clinical trial is underway.
First batch of awardees announced for new Chief Scientific Officer small grant program
Research projects of the winners – 12 of 23 were awarded funding – range from virtual reality training to the use of AI to predict COVID-19.







