The center becomes the first in the country to administer a commercial gene therapy infusion to treat Hemophilia A, the common disorder affecting males.
Parent provides powerful testimony at second-annual CHOC and UCI Rare Disease Symposium & Family Conference
At the annual symposium, hundreds will gather to share about advances in rare disease research and a unifying theme: hope.
CHOC doctors discover the possible efficacy of treating PCS with the GI device IB-Stim. A clinical trial is underway.
Research projects of the winners – 12 of 23 were awarded funding – range from virtual reality training to the use of AI to predict COVID-19.
A CHOC hematologist and prolific author on innovative medicine, Dr. Diane Nugent joins the executive committee of NHLBI’s CONNECTS.