The novel work of the new advanced bronchoscopy team ended up dramatically shortening what would have been a much longer hospital stay and likely prevented the 8-year-old from having to undergo a surgical intervention.
Ushering in a new era for sickle cell disease treatment
The 2025 administration of gene therapy to treat sickle cell disease marked more than an historic first for Rady Children’s Health Orange County. It also changed the trajectory of a young adult’s life and capped a two-decade journey for the physician and the hematology team who delivered it.
Boy, 8, is first in region to receive new gene therapy for Duchenne muscular dystrophy
A third patient is scheduled to receive the FDA-approved therapy, with some patients showing improvement in their function and motor skills.
Girl, 3, is thriving after innovative surgical approach to repair her defective heart
A two-stage approach was devised for Taylor, whose left ventricle was too underdeveloped for her aortic arch to be repaired straight away.
Neurosurgery-orthopedics partnership yields strong outcomes for complex spinal patients
Born with spina bifida, Sophia’s sunny space and disposition give no clue to her challenging childhood.
National brain mapping study receives its first ‘magical’ gift from patient with cancer
Ethan Nguyen is the first pediatric patient to become part of an NIH-funded study that began in 2022 and is led by UC Irvine.
