Grant’s support will help advance gene-therapy treatment for the rare lysosomal storage disease mucopolysaccharidosis type I (MPS I).
Young leukemia patient is part of several oncology research studies
Max, CHOC patient with acute lymphoblastic leukemia (ALL), participates in cancer research trials to improve outcomes and treatments.
Kazaam! Comic Assent earns kudos as tool for young patients to better grasp research studies
Colorful comics aid young patients in understanding and providing assent for participation in research studies to advance treatments.
‘We will have a better tomorrow for these kids’
Parent provides powerful testimony at second-annual CHOC and UCI Rare Disease Symposium & Family Conference
CHOC awarded coveted NIH grant for research into hydrocephalus treatment
CHOC’s hydrocephalus research laboratory team receives grant that could lead to improvements in care for a debilitating and complex disease.
Second-annual CHOC-UCI Rare Diseases Symposium set for March 10, 2023
At the annual symposium, hundreds will gather to share about advances in rare disease research and a unifying theme: hope.
