CHOC Pediatrica
News and Information for Pediatric Healthcare Professionals
The 2025 administration of gene therapy to treat sickle cell disease marked more than an historic first for Rady Children’s Health Orange County. It also changed the trajectory of a young adult’s life and capped a two-decade journey for the physician and the hematology team who delivered it.
Through a combination of formal instruction, mentorship, shadowing, and active participation in research activities, the CRC interns gained practical skills that cannot be fully taught in a classroom setting or abbreviated program.
Learn how Rady Children’s Health Orange County investigates gene therapy to treat childhood diseases, including Hurler syndrome, liver cancer and more.
Discover how Rady Children’s Health Orange County is studying gene therapy as a less burdensome treatment alternative for children with Hurler syndrome.
While many AI conferences exist, few focus specifically on pediatric care, developmental biology, and the long-term impact of childhood conditions across the lifespan.
The research of Dr. Assaf and UCI Professor Jun Wu produced groundbreaking work at the intersection of climate change, mental health, and pediatric emergency medicine.
