The recent discovery of a previously unknown fusion gene in acute myeloid leukemia (AML) is shifting current thinking about cancer’s dynamic nature and the drivers of relapse, with implications for customized treatment.
Confronting the potential for a return of a rare measles sequela
As measles cases in the U.S. rise, a complication called SSPE may become more common. Learn about a recent case that prompts questions about how to respond.
Ushering in a new era for sickle cell disease treatment
The 2025 administration of gene therapy to treat sickle cell disease marked more than an historic first for Rady Children’s Health Orange County. It also changed the trajectory of a young adult’s life and capped a two-decade journey for the physician and the hematology team who delivered it.
First clinical research coordinator interns graduate from novel pediatric hospital program
Through a combination of formal instruction, mentorship, shadowing, and active participation in research activities, the CRC interns gained practical skills that cannot be fully taught in a classroom setting or abbreviated program.
Shaping the future of pediatric gene therapy
Learn how Rady Children’s Health Orange County investigates gene therapy to treat childhood diseases, including Hurler syndrome, liver cancer and more.
‘Something better’? Gene therapy’s potential to treat Hurler syndrome
Discover how Rady Children’s Health Orange County is studying gene therapy as a less burdensome treatment alternative for children with Hurler syndrome.
